| Issue Date | Title | Author(s) | Relation | scopus | WOS | Fulltext/Archive link |
|---|---|---|---|---|---|---|
| 2002 | Efficacy of gene therapy for a prototypical lysosomal storage disease (GSD-II) is critically dependent on vector dose, transgene promoter, and the tissues targeted for vector transduction | Ding, E.; Hu, H.; Hodges, B. L.; Migone, F.; Serra, D.; Xu, F.; Chen, Y. T.; Amalfitano, A. | Mol Ther 5, 436-446 |
